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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
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Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Knockout
Hear
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
CD38
Autophagy
Morphogenesis
DHPR α1S
Muscle development
Muscle Biology
Becker BMD muscular dystrophy
Cardiomyopathie
Inbred C57BL
Metabolism
Becker muscular dystrophy BMD
Male
Dystrophin
Inbred mdx
Mice
Energy Metabolism/drug effects
DMD
Mitochondrial fission
Gene expression
Muscle Strength
Duchenne DMD dystrophy
Cell Line
Dystrophin central domain
Cell Biology
Centronuclear myopathy
Dystrophin-EGFP
Dynamin 2
Dystrophie Musculaire de Duchenne DMD
DMO
Cells
Myogenesis
Exon skipping
Homeostasis
L-Type
Animals
Ex-vivo
Drp1
Skeletal muscle
Calcium
Cachexia
Muscular dystrophy
Cardiomyopathy
Animal/physiopathology
Antisense oligonucleotides
Multi exon skipping
Molecular docking
Duchenne muscular dystrophy DMD
Dystrophie musculaire de Becker
Long noncoding RNA
Liver
Genomic
Diseases
CaVβs
Duchenne muscular dystrophy
Mdx mouse
BMD
Gene modifiers
Muscle
Gene Expression Regulation/drug effects
CTNNB1
CaV subunits
LncARN
Multiresolution modeling
Cultured
Myotendinous junction
Clinical trials
Human Umbilical Vein Endothelial Cells
MiARN
Multi resolution modeling
Allele‐specific silencing therapy
Epigenetics
Long QT
Génomique
Muscular Atrophy
Muscular Dystrophy
Immunoglobulin Fc Fragments/pharmacology
Inhibitors
Activin Receptors
MES
Delivery
Becker muscular dystrophy
Dystrophine
Base Sequence
Cell homeostasis
Muscles/physiopathology
Dystrophy
Calcium Channels
LncRNA
NNOS
Humans
Invivo
NAD+
Dystrophie Musculaire de Becker BMD
Modificateurs de gènes
Molecular Sequence Data
Hepatocellular carcinoma
LKB1